Nusinersen for Adults with Spinal Muscular Atrophy: Clinical Effectiveness

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Project Status:
Completed
Project Line:
Reference List
Project Sub Line:
Reference List
Project Number:
RA1089-000

Question

  1. What is the clinical effectiveness of nusinersen for adults with spinal muscular atrophy?

Key Message

Two non-randomized studies regarding the clinical effectiveness of nusinersen for adults with spinal muscular atrophy were identified. ​